Antisense oligonucleotide treatment following viral delivery of artificial SOD1-targeting miRNA shows improved efficacy in SOD1-G93A mice.

@article{hawley2026antisense,
author = {Hawley, Zachary C.E. and Guise, Amanda J. and Pardo, Ingrid D. and Chowdhury, Twinkle and Hana, Sam and Zavodszky, Maria I. and Engle, Linda and Wiltberger, Kelly and Bartlett, Dan and Raitcheva, Denitza and Bommegowda, Santhosh and Lee, Wan-Hung and Chen, Shukkwan K. and Sheehy, Adam and Driscoll, Rachelle and Peterson, Michael and Sebalusky, Jennifer and Hamann, Stefan and Marsh, Galina and Doherty, Jessica and Chicoine, Kay-Ellen and Cundiff, Paige and Dwyer, Sean and Clarner, Pete and Zeng, Weike and Ferretti, Daniel and Tuczkewycz, Taras and Isaza, Isabel and Patrovanie, Melissa and Mcgladrigan, Collin and Chu, Jenhwa and Morrison, James P. and Arnold, H. Moore and Shen, Shen and Hurt, Jessica A. and Trapa, Patrick and Graham, Danielle L. and Plowey, Edward D. and Lo, Shih-Ching},
title = {{Antisense oligonucleotide treatment following viral delivery of artificial SOD1-targeting miRNA shows improved efficacy in SOD1-G93A mice}},
journal = {Molecular therapy. Advances},
year = {2026},
month = jul,
volume = {34},
number = {3},
pages = {201818},
publisher = {American Society of Gene \& Cell Therapy},
issn = {3117-387X},
doi = {10.1016/j.omta.2026.201818},
url = {https://doi.org/10.1016/j.omta.2026.201818},
pmid = {42620667},
pmcid = {PMC13486805}
}

TY - JOUR
AU - Hawley, Zachary C.E.
AU - Guise, Amanda J.
AU - Pardo, Ingrid D.
AU - Chowdhury, Twinkle
AU - Hana, Sam
AU - Zavodszky, Maria I.
AU - Engle, Linda
AU - Wiltberger, Kelly
AU - Bartlett, Dan
AU - Raitcheva, Denitza
AU - Bommegowda, Santhosh
AU - Lee, Wan-Hung
AU - Chen, Shukkwan K.
AU - Sheehy, Adam
AU - Driscoll, Rachelle
AU - Peterson, Michael
AU - Sebalusky, Jennifer
AU - Hamann, Stefan
AU - Marsh, Galina
AU - Doherty, Jessica
AU - Chicoine, Kay-Ellen
AU - Cundiff, Paige
AU - Dwyer, Sean
AU - Clarner, Pete
AU - Zeng, Weike
AU - Ferretti, Daniel
AU - Tuczkewycz, Taras
AU - Isaza, Isabel
AU - Patrovanie, Melissa
AU - Mcgladrigan, Collin
AU - Chu, Jenhwa
AU - Morrison, James P.
AU - Arnold, H. Moore
AU - Shen, Shen
AU - Hurt, Jessica A.
AU - Trapa, Patrick
AU - Graham, Danielle L.
AU - Plowey, Edward D.
AU - Lo, Shih-Ching
TI - Antisense oligonucleotide treatment following viral delivery of artificial SOD1-targeting miRNA shows improved efficacy in SOD1-G93A mice
T2 - Molecular therapy. Advances
J2 - Mol Ther Adv
PY - 2026
DA - 2026/07/24
VL - 34
IS - 3
SP - 201818
SN - 3117-387X
PB - American Society of Gene & Cell Therapy
DO - 10.1016/j.omta.2026.201818
UR - https://doi.org/10.1016/j.omta.2026.201818
LA - en
ER -

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