Exosome-like nanovesicles from acerola for CRISPR-Cas9 ribonucleoprotein delivery to the central nervous system.
Overview
- Department of Molecular Pathology, Tokyo Medical University, Tokyo, Japan
- Department of Pharmacology, Tokyo Medical University, Tokyo, Japan
- Department of Molecular and Cellular Medicine, Institute of Medical Science, Tokyo Medical University, Tokyo, Japan
Abstract
An aberrant six-base repeat in intron 1 of C9orf72 is the most frequent cause of solitary and familial amyotrophic lateral sclerosis and frontotemporal dementia. This mutation is a potential target for CRISPR/
Reproduced under the paper's license (CC BY), from the paper cited above.
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Versions
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Version 1, 30 September 2026: the first record
Recorded: type, language, journal, volume, issue, pages, dates, 9 authors, 8 keywords, 1 funder, 34 references.
Cite
This paper
Nagamatsu, Y., Umezu, T., Hong, T., Niijima, T., Ohno, S.-i., Harada, Y., Kanekura, K., Ochiya, T., & Kuroda, M. (2026). Exosome-like nanovesicles from acerola for CRISPR-Cas9 ribonucleoprotein delivery to the central nervous system. Molecular therapy. Nucleic acids, 37(2), 102896. https://
BibTeX
@article{nagamatsu2026ex
author = {Nagamatsu, Yui and Umezu, Tomohiro and Hong, Taehun and Niijima, Takahide and Ohno, Shin-ichiro and Harada, Yuichiro and Kanekura, Kohsuke and Ochiya, Takahiro and Kuroda, Masahiko},
title = {{Exosome-like nanovesicles from acerola for CRISPR-Cas9 ribonucleoprotein delivery to the central nervous system}},
journal = {Molecular therapy. Nucleic acids},
year = {2026},
month = mar,
volume = {37},
number = {2},
pages = {102896},
publisher = {American Society of Gene \& Cell Therapy},
issn = {2162-2531},
doi = {10.1016/
url = {https://
pmid = {41909467},
pmcid = {PMC13022685}
}
RIS
TY - JOUR
AU - Nagamatsu, Yui
AU - Umezu, Tomohiro
AU - Hong, Taehun
AU - Niijima, Takahide
AU - Ohno, Shin-ichiro
AU - Harada, Yuichiro
AU - Kanekura, Kohsuke
AU - Ochiya, Takahiro
AU - Kuroda, Masahiko
TI - Exosome-like nanovesicles from acerola for CRISPR-Cas9 ribonucleoprotein delivery to the central nervous system
T2 - Molecular therapy. Nucleic acids
J2 - Mol Ther Nucleic Acids
PY - 2026
DA - 2026/
VL - 37
IS - 2
SP - 102896
SN - 2162-2531
PB - American Society of Gene & Cell Therapy
DO - 10.1016/
UR - https://
LA - en
ER -
CSL-JSON
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"author": [
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"family": "Nagamatsu",
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"ISSN": "2162-2531",
"publisher": "American Society of Gene & Cell Therapy",
"URL": "https://
"language": "en",
"issued": {
"date-parts": [
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}
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